BrainStorm Gains Orphan Drug Designation
BrainStorm Cell Therapeutics has received orphan drug designation for the treatment of amyotrophic lateral sclerosis.
BrainStorm Cell Therapeutics has received orphan drug designation from the US FDA for NurOwn, the company's autologous adult stem cell product candidate for the treatment of amyotrophic lateral sclerosis. BrainStorm president Chaim Lebovits said the company is extremely pleased to have been granted the benefits of orphan drug designation as it continues to advance NurOwn as a potential new treatment for amyotrophic lateral sclerosis.
The company is planning to conduct clinical trials of NurOwn in the first half of 2011.
"Because of the safety profile with autologous adult stem cells, potential for intramuscular or intrathecal administration and multiple mechanisms of action, we feel this product candidate could effectively address the needs of patients with amyot
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