Miglustat

Miglustat
Product Description

Miglustat is a rare drug used majorly for the treatment of Gaucher's disease, (a condition in which a certain fatty substance is not broken down normally in the body and instead builds up in some organs and causes liver, spleen, bone, and blood problems). Miglustat is in a class of medications called enzyme inhibitors. Miglustat is now the first and only approved therapy for patients with Niemann-Pick disease type C (NP-C). It has recently been approved for treatment of progressive neurological symptoms in adult and pediatric patients in the European Union, Brazil, and South Korea.

US DMF filing planned in Q4 2021. product manufactured in a US FDA approved facility. 


Available form: API
Planned : Capsules

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Apothecon Pharmaceuticals

  • IN
  • 2018
    On CPHI since
View company profile
Specifications
  • CAS Registry Number
    72599-27-0
  • Supplied from
    India
More specifications Fewer specifications

Apothecon Pharmaceuticals

  • IN
  • 2018
    On CPHI since
View company profile

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